lunsohttps parvec
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Indications
- severe-to-profound sensorineural hearing loss in adults & children with biallelic variants in the otoferlin (OTOF) gene & preserved outer hair cell function with no prior cochlear implant in the same ear.
Mechanism of action
- adenovirus-associated vector-based gene therapy
References
- ↑ Monaco K First Gene Therapy Approved for Hearing Loss Maker says Otarmeni will be offered for free in the U.S. MedPage Today. April 23, 2026 https://www.medpagetoday.com/genetics/generalgenetics/120935