etranacogene dezaparvovec-drlb (Hemgenix)

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* Hemgenix can be administered only once[2]

provided in kits containing 10 to 48 single-use vials, each kit constituting a dosage unit based on the patient's weight

10 mL etranacogene dezaparvovec-drlb 10E13 VECTOR-GENOMES/mL Injection


* condider glucocorticoid for elevated serum ALT[2]

Adverse effects

Mechanism of action

More general terms


  1. Shah J, Kim h, Sivamurthy K et al Comprehensive analysis and prediction of long-term durability of factor IX activity following etranacogene dezaparvovec gene therapy in the treatment of hemophilia B. Curr Med Res Opin. 2023 Feb;39(2):227-237. PMID:
  2. 2.0 2.1 2.2 2.3 2.4 HIGHLIGHTS OF PRESCRIBING INFORMATION Hemgenix <TM> (etranacogene dezaparvovec-drlb) suspension, for intravenous infusion