risdiplam (Evrysdi)
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Indications
- treatment of spinal muscular atrophy
Contraindications
Dosage
60 mg of risdiplam powder for constitution to provide 0.75 mg/mL solution
Adverse effects
Mechanism of action
- survival of motor neuron 2 (SMN2) splicing modifier
More general terms
References
- ↑ Johnson K Risdiplam Promising for Spinal Muscular Atrophy. Medscape - Mar 09, 2021. https://www.medscape.com/viewarticle/947139
- ↑ Baranello G, Darras BT, Day JW et al Risdiplam in Type 1 Spinal Muscular Atrophy N Engl J Med 2021; 384:915-923 PMID: https://www.ncbi.nlm.nih.gov/pubmed/33626251 https://www.nejm.org/doi/full/10.1056/NEJMoa2009965
- ↑ Highlights of prescribing information Evrysdi (risdiplam) for oral solution https://www.gene.com/download/pdf/evrysdi_prescribing.pdf