venglustat; ibiglustat

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Contraindications

Mechanism of action

More general terms

References

  1. Giladi N et al. Safety and efficacy of venglustat in GBA1-associated Parkinson's disease: An international, multicentre, double-blind, randomised, placebo-controlled, phase 2 trial. Lancet Neurol 2023 Aug; 22:661. PMID: https://pubmed.ncbi.nlm.nih.gov/37479372 https://www.thelancet.com/journals/laneur/article/PIIS1474-4422(23)00205-3/fulltext

Database