ezutromid
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Indications
- Duchenne muscular dystrophy (investigative agent)
Mechanism of action
- utrophin modulator
- may act as functional replacement for dystrophin
- diminishes inflammation in calf muscles of children with Duchenne muscular dystrophy
More general terms
References
- ↑ George J, Ezutromid Shows Potential in DMD. Phase II study indicates modulating utrophin may reduce muscle inflammation. MedPage Today. April 29, 2018 https://www.medpagetoday.com/meetingcoverage/aan/72591
Muntoni F, et al Ezutromid significantly reduced muscle damage whilst maintaining utrophin in patients with Duchenne muscular dystrophy (DMD) after 24-weeks of treatment. Anerican Academy of Neurology (AAN) 2018.