CFTR gene-liposome complex

^[1]

Dosage

contains normal working copy of CFTR gene delivered in liposomal complex by nebulizer^[1]

↑ ^1.0 ^1.1 ^1.2 Alton EW, Armstrong DK, Ashby D et al Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial. Lancet. July 3, 2015 <PubMed> PMID: https://www.ncbi.nlm.nih.gov/pubmed/26149841 <Internet> http://www.thelancet.com/pdfs/journals/lanres/PIIS2213-2600%2815%2900245-3.pdf